“If you have a rare disease, it’s not rare to you.”

In this episode, Dr. Naveen Pemmaraju of MD Anderson Cancer Center in Houston, TX, sheds light on the latest treatment advancements for myelofibrosis. The pace of scientific discovery for rare diseases is moving at a fast rate, resulting in better outcomes for myelofibrosis patients.

*This episode was recorded on Rare Disease Day, February 29, 2024

Mentioned on this episode: 

• Myelofibrosis
  
  
• Myeloproliferative Neoplasms (MPNs)
  
  
• Acute Myeloid Leukemia
  
  
• CAR T-cell Therapy
  
  
• Immunotherapy Fact Sheet (Bispecific Antibodies)
  
  
• Stem Cell Transplant
  
  
• TRANSFORM-1 trial
  
  
• American Society of Hematology (ASH)
  

Additional LLS Support Resources: 

• Information Specialists 
  
  
• Financial support
  
  
• Free telephone/web patient programs 
  
  
• Free booklets 
  
  
• Clinical Trial Support Center
  
  
• Young Adult Resources
  
  
• Caregiver support 
  
  
• Caregiver Workbook
  
  
• Survivorship Workbook
  
  
• Online chats 
  
  
• LLS Community 
  
  
• Support groups 
  
  
• Patti Robinson Kaufmann First Connection Program 
  
  
• Free Nutrition Consultations
  

Support for this episode provided by: GSK plc.

The post Hope for a Rare Disease: Myelofibrosis first appeared on The Bloodline with LLS.

The post Hope for a Rare Disease: Myelofibrosis appeared first on The Bloodline with LLS.